Practice Leber’s Congenital Amaurosis (LCA) - 3.3.1 | Gene Therapy and Clinical Applications | Genetic Engineering Advance
Students

Academic Programs

AI-powered learning for grades 8-12, aligned with major curricula

Professional

Professional Courses

Industry-relevant training in Business, Technology, and Design

Games

Interactive Games

Fun games to boost memory, math, typing, and English skills

Leber’s Congenital Amaurosis (LCA)

3.3.1 - Leber’s Congenital Amaurosis (LCA)

Enroll to start learning

You’ve not yet enrolled in this course. Please enroll for free to listen to audio lessons, classroom podcasts and take practice test.

Learning

Practice Questions

Test your understanding with targeted questions

Question 1 Easy

What genetic condition does LCA represent?

💡 Hint: Think about vision-related genetic disorders.

Question 2 Easy

What does Luxturna target in gene therapy?

💡 Hint: Consider which gene is deficient in some LCA cases.

4 more questions available

Interactive Quizzes

Quick quizzes to reinforce your learning

Question 1

What is LCA primarily known for?

Bone degeneration
Vision Impairment
Heart problems

💡 Hint: Focus on the primary symptom of the disorder.

Question 2

Luxturna is designed to help which gene?

RPE65
CFTR
SMN1

💡 Hint: This gene is specifically linked to a type of retinal disorder.

2 more questions available

Challenge Problems

Push your limits with advanced challenges

Challenge 1 Hard

Propose a plan for addressing cost barriers in administering Luxturna to a broader population.

💡 Hint: Think of collaborative and innovative funding methods.

Challenge 2 Hard

Analyze the impact of Luxturna on the future of genetic disorders treatment.

💡 Hint: Consider how breakthroughs influence policy and societal views.

Get performance evaluation

Reference links

Supplementary resources to enhance your learning experience.