3.3.2 - Spinal Muscular Atrophy (SMA)
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Practice Questions
Test your understanding with targeted questions
What does SMA stand for?
💡 Hint: Think about the long form of the acronym.
What is the role of the SMN protein?
💡 Hint: Remember its name when recalling its function.
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Interactive Quizzes
Quick quizzes to reinforce your learning
What does SMA stand for?
💡 Hint: It’s about muscles and how they function.
True or False: Zolgensma works by providing the body with a functional copy of the SMN1 gene.
💡 Hint: Think about the purpose of gene therapy.
2 more questions available
Challenge Problems
Push your limits with advanced challenges
Propose a clinical trial design to test a new gene therapy for SMA and discuss its ethical ramifications.
💡 Hint: Think about the importance of ethical oversight in medical research.
Analyze the cost implications of Zolgensma in relation to its benefits for the healthcare system.
💡 Hint: Consider both short-term and long-term financial impacts.
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