Practice Spinal Muscular Atrophy (SMA) - 3.3.2 | Gene Therapy and Clinical Applications | Genetic Engineering Advance
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Practice Questions

Test your understanding with targeted questions related to the topic.

Question 1

Easy

What does SMA stand for?

💡 Hint: Think about the long form of the acronym.

Question 2

Easy

What is the role of the SMN protein?

💡 Hint: Remember its name when recalling its function.

Practice 4 more questions and get performance evaluation

Interactive Quizzes

Engage in quick quizzes to reinforce what you've learned and check your comprehension.

Question 1

What does SMA stand for?

  • A) Spinal Muscular Atrophy
  • B) Surviving Muscle Neurons
  • C) Spinal Motor Neuron Association

💡 Hint: It’s about muscles and how they function.

Question 2

True or False: Zolgensma works by providing the body with a functional copy of the SMN1 gene.

  • True
  • False

💡 Hint: Think about the purpose of gene therapy.

Solve 2 more questions and get performance evaluation

Challenge Problems

Push your limits with challenges.

Question 1

Propose a clinical trial design to test a new gene therapy for SMA and discuss its ethical ramifications.

💡 Hint: Think about the importance of ethical oversight in medical research.

Question 2

Analyze the cost implications of Zolgensma in relation to its benefits for the healthcare system.

💡 Hint: Consider both short-term and long-term financial impacts.

Challenge and get performance evaluation